Takaisin

What is the effectiveness of PCSK9 inhibitors for cardiovascular disease (CVD) prevention?

Näytönastekatsaukset
Miia Aro
24.9.2026

Level of evidence: A

In adult, high risk CVD patients with high LDL-C, PCSK9 inhibitors alirocumab and evolocumab in addition to statin or life-style counselling reduce the risk of cardiovascular endpoint events (alirocumab events 11 % vs. 14 % in placebo, evolocumab 7 % vs. 11 %), any myocardial infarction (alirocumab events 10 % vs. 12 % in placebo, evolocumab 3.2 % vs. 4.5 %), or any stroke (alirocumab events 1.1% vs. 1.6 % in placebo, evolocumab 1.5 % vs. 1.9 %).

Alirocumab reduces the risk of CVD with absolute difference of 3% compared to placebo, and in evolocumab with 4%. In addition, alirocumab reduces all-cause mortality in these patients but evolocumab did not. However, the follow-up times were quite short. There is very limited evidence on any potential safety issues or adverse effects of both evolocumab and alirocumab.

Table 1. Description of the included studies
Reference Study type Population Intervention and comparison Outcomes Risk of bias «Additional comments for included studies...»2
SR=systematic review, RCT=randomised controlled trial, CVD=cardiovascular disease
«Schmidt AF, Carter JL, Pearce LS, ym. PCSK9 monocl...»1 SR 24 RCTs with data on 60 997 participants. People at high risk of CVD (history of CVD or high LDL-C despite treatment) in outpatient settings. Alirocumab or evolocumab vs. placebo or active treatment 1.CVD endpoint
2.All-cause mortality
3.Myocardial infarction
4.Any stroke
Low
Table 2. Additional comments for included studies
Reference Comments
«Schmidt AF, Carter JL, Pearce LS, ym. PCSK9 monocl...»1 18 trials studied alirocumab and 6 evolocumab. All participants received background lipid-lowering treatment or lifestyle counselling. Six alirocumab studies used an active treatment comparison group (the remaining used placebo), and 3 evolocumab trials used active comparison. Follow-up ranged from 6 to 36 months for the comparisons with placebo and from 6 to 12 months for comparisons with active treatment. Most of the available studies preferentially enrolled people with either established CVD or at a high risk already.

Results

Table 3. Composite endpoint of CVD, defined as urgent coronary revascularisation, unstable angina pectoris, non-fatal and fatal myocardial infarction, non-fatal and fatal stroke, and CHD death.
Reference Number of studies and number of patients (I/C) Follow-up time Absolute number of events (%) I Absolute number of events (%) C Odds ratio (95% CI)
Level of evidence: high
CVD=cardiovascular disease; CHD=coronary heart disease; I=intervention; C=comparison; CI=confidence interval
«Schmidt AF, Carter JL, Pearce LS, ym. PCSK9 monocl...»1 alirocumab
10 studies, 23868 patients (12770/11098)
6-36 months 1411 (11 %) 1531 (14%) 0.87 (0.80,0.94)
evolocumab.
3 studies, 29432 patients (14867/14565)
1049 (7%) 1639 (11%) 0.84 (0.78, 0.91)
Table 4. All-cause mortality
Reference Number of studies and number of patients (I/C) Follow-up time Absolute number of events (%) I Absolute number of events (%) C Odds Ratio (95% CI)
Level of evidence: moderate
The quality of evidence is downgraded due to imprecision and indirectness (short follow-up time).
I=intervention; C=comparison; CI=confidence interval
«Schmidt AF, Carter JL, Pearce LS, ym. PCSK9 monocl...»1 alirocumab
12 studies, 24797 patients (13390/11407)
6-36 months 352 (2.6 %) 408 (3.6 %) 0.83 (0.72,0.96)
evolocumab
3 studies, 29432 patients (14867/14565)
449 (3.02 %) 430 (2.95 %) 1.04 (0.91,1.19)
Table 5. Myocardial infarction
Reference Number of studies and number of patients (I/C) Follow-up time Absolute number of events (%) I Absolute number of events (%) C Odds ratio (95% CI)
Level of evidence: high
I=intervention; C=comparison; CI=confidence interval
«Schmidt AF, Carter JL, Pearce LS, ym. PCSK9 monocl...»1 alirocumab
9 studies, 23352 patients (12369/10983)
6-36 months 1221 (10 %) 1372 (12 %) 0.86 (0.79,0.94)
evolocumab
3 studies, 29432 patients (14867/14565)
479 (3.2 %) 653 (4.5 %) 0.72 (0.64,0.82)
Table 6. Any stroke
Reference Number of studies and number of patients (I/C) Follow-up time Absolute number of events (%) I Absolute number of events (%) C Odds Ratio (95% CI)
Level of evidence: high
I=intervention; C=comparison; CI=confidence interval
«Schmidt AF, Carter JL, Pearce LS, ym. PCSK9 monocl...»1 alirocumab
8 studies, 22835 patients (12024/10811)
6-36 months 135 (1.1%) 176 (1.6%) 0.73 (0.58,0.91)
evolocumab
2 studies, 28531 patients (14268/14263)
209 (1.5%) 265 (1.9%) 0.79 (0.65, 0.94)

References

  1. Schmidt AF, Carter JL, Pearce LS, ym. PCSK9 monoclonal antibodies for the primary and secondary prevention of cardiovascular disease. Cochrane Database Syst Rev 2020;10(10):CD011748 «PMID: 33078867»PubMed